Dock8 Deficiency
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CLINICAL_TRIALS research · 2026-04-24Clinical Trial Update: Establishing Fibroblast-Derived Cell Lines From Skin Biopsies of Patients With Immunodeficiency or Immunodysregulation Disorders
A National Institute of Allergy and Infectious Diseases trial update describes establishing fibroblast-derived cell lines from skin biopsies…
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CLINICAL_TRIALS research · 2026-04-24Clinical Trial Update: Apheresis of Patients With Immunodeficiency
An NCI-sponsored clinical trial evaluating apheresis in patients with immunodeficiencies including leukocyte adhesion deficiency type 1, DOC…
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CLINICAL_TRIALS trial_result · 2026-04-16Clinical Trial Update: Pilot Study of Reduced-Intensity Hematopoietic Stem Cell Transplant of DOCK8 Deficiency [Phase 2]
Phase 2 pilot study evaluating reduced-intensity hematopoietic stem cell transplantation for DOCK8 deficiency; the trial is currently active…