Debrancher Deficiency

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CLINICAL_TRIALS trial_result · 2024-02-22
Clinical Trial Update: The Effect of Triheptanoin on Fatty Acid Oxidation and Exercise Tolerance in Patients With Glycogenoses [Phase 2]
Phase 2 trial assessing the effect of triheptanoin on fatty acid oxidation and exercise tolerance in patients with Tarui disease and debranc…