Ctnnb1 Neurodevelopmental Syndrome
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CLINICAL_TRIALS research · 2026-03-25Clinical Trial Update: Gene Replacement Therapy for Treatment of Paediatric Patients With CTNNB1 Neurodevelopmental Syndrome [Phase 1, Phase 2]
Ongoing Phase 1/2 gene replacement therapy trial in pediatric patients with CTNNB1 neurodevelopmental syndrome; recruitment is currently ong…
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CLINICAL_TRIALS research · 2025-09-22Clinical Trial Update: CTNNB1 Neurodevelopmental Syndrome - Natural History Study
A natural history study of CTNNB1 neurodevelopmental syndrome is currently recruiting participants to characterize the condition over time.