Crigler-najjar Syndrome
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Sign up freeTop drugs studied for this disease
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CLINICAL_TRIALS trial_result · 2024-12-03Clinical Trial Update: Efficacy and Safety of GNT0003 Following Imlifidase Pre-treatment in Severe Crigler-Najjar Syndrome [Phase 2]
Phase 2 study evaluating GNT0003 after imlifidase pre-treatment in severe Crigler-Najjar syndrome is currently recruiting.
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CLINICAL_TRIALS trial_result · 2024-05-29Clinical Trial Update: HepaStem Long-Term Safety Registry
This clinical trial update announces the termination of the HepaStem long-term safety registry and highlights conditions studied (urea cycle…
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CLINICAL_TRIALS trial_result · 2020-10-19Clinical Trial Update: Safety Study of HepaStem for the Treatment of Urea Cycle Disorders (UCD) and Crigler-Najjar Syndrome (CN) [Phase 1, Phase 2]
Phase 1/2 safety study of HepaStem for urea cycle disorders and Crigler-Najjar syndrome has completed.
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CLINICAL_TRIALS trial_result · 2019-02-06Clinical Trial Update: Clinical Assessment Study in Crigler-Najjar Syndrome
Completed clinical assessment study in Crigler-Najjar syndrome sponsored by Audentes Therapeutics.
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CLINICAL_TRIALS trial_result · 2017-12-13Clinical Trial Update: Immunity Against AAV in Crigler Najjar Patient
A Genethon-sponsored trial update reports on immune responses to an AAV vector in a Crigler-Najjar syndrome patient. The study status is com…
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CLINICAL_TRIALS trial_result · 2007-04-18Clinical Trial Update: Orlistat Treatment of Crigler-Najjar Disease [NA]
A completed clinical trial evaluating Orlistat for Crigler-Najjar syndrome sponsored by University Medical Center Groningen has finished. Th…