Congenital Myasthenic Syndromes
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CLINICAL_TRIALS research · 2026-02-27Clinical Trial Update: A Prospective Natural History and Outcome Measure Validation Study of Congenital Myasthenic Syndromes
A prospective natural history study and outcome measure validation study focused on congenital myasthenic syndromes, currently recruiting.
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CLINICAL_TRIALS research · 2025-01-20Clinical Trial Update: Treatment Use of 3,4-Diaminopyridine
This clinical trial update discusses the use of 3,4-diaminopyridine for congenital myasthenic syndromes, noting that the study is no longer …
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CLINICAL_TRIALS trial_result · 2021-04-02Clinical Trial Update: Amifampridine Phosphate for the Treatment of Congenital Myasthenic Syndromes [Phase 3]
Phase 3 trial of amifampridine phosphate for congenital myasthenic syndromes has completed with results posted.
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CLINICAL_TRIALS research · 2007-10-10Clinical Trial Update: Ephedrine for the Treatment of Congenital Myasthenia [Phase 1, Phase 2]
This document notes a Phase 1/Phase 2 clinical trial evaluating ephedrine for the treatment of congenital myasthenic syndromes.