Congenital Dyserythropoietic Anemia Type Ii
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CLINICAL_TRIALS research · 2025-07-08Clinical Trial Update: To Assess Safety of Mitapivat and Provide Proof of Concept of the Efficacy of the Drug in Patients With RBC Membranopathies or CDAII. [Phase 2]
A Phase 2 clinical trial is underway to evaluate the safety of mitapivat and provide proof-of-concept of its efficacy in patients with RBC m…