Congenital Adrenal Hyperplasia
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Sign up freeTop drugs studied for this disease
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CLINICAL_TRIALS trial_result · 2021-02-17Clinical Trial Update: A Study of ATR-101 for the Treatment of Congenital Adrenal Hyperplasia [Phase 2]
Phase 2 trial update for ATR-101 in congenital adrenal hyperplasia has completed with results posted.
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FDA approval · 2020-09-29FDA Approved: ALKINDI SPRINKLE — Original Application (Eton Pharmaceuticals, Inc.)
FDA approves ALKINDI SPRINKLE (hydrocortisone granules) from an original NDA by Eton Pharmaceuticals, providing hydrocortisone replacement t…
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CLINICAL_TRIALS trial_result · 2020-09-02Clinical Trial Update: Comparisons of Different Forms of Glucocorticoid on the Recovery of Reproductive Function in Patients With 21α-hydroxylase Deficiency [Phase 4]
Phase 4 trial comparing different glucocorticoid formulations for recovery of reproductive function in congenital adrenal hyperplasia.
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CLINICAL_TRIALS trial_result · 2019-09-04Clinical Trial Update: Comparison of Chronocort® With Standard Glucocorticoid Therapy in Patients With Congenital Adrenal Hyperplasia [Phase 3]
A Phase 3 trial comparing Chronocort with standard glucocorticoid therapy in congenital adrenal hyperplasia has completed with results poste…
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CLINICAL_TRIALS trial_result · 2017-11-22Clinical Trial Update: Comparison of Cortisol Pump With Standard Treatment for Congenital Adrenal Hyperplasia [Phase 2]
Phase 2 clinical trial comparing cortisol pump with standard treatment for congenital adrenal hyperplasia completed; results posted in 2017.
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CLINICAL_TRIALS trial_result · 2017-07-02Clinical Trial Update: Catecholamine Reserve and Exercise Tolerance in Healthy Volunteers and Patients With Congenital Adrenal Hyperplasia
This clinical trial update reports on catecholamine reserve and exercise tolerance in healthy volunteers and patients with congenital adrena…
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CLINICAL_TRIALS trial_result · 2017-05-22Clinical Trial Update: Growth Hormone (GH) in Congenital Adrenal Hyperplasia
This clinical trial update notes the completion of a study evaluating growth hormone therapy in patients with congenital adrenal hyperplasia…
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CLINICAL_TRIALS trial_result · 2017-05-17Clinical Trial Update: Pilot Study to Characterize and Examine the Pharmacokinetics and Efficacy of Chronocort® in Adults With CAH [Phase 2]
A Phase 2 pilot trial of Chronocort in adults with congenital adrenal hyperplasia completed, with results evaluating pharmacokinetics and ef…
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CLINICAL_TRIALS trial_result · 2017-02-14Clinical Trial Update: A Two-part, Study to Compare the Pharmacokinetics and Dose Proportionality of up to 6 Chronocort Formulations [Phase 1]
Phase 1 study evaluating the pharmacokinetics and dose proportionality of up to six Chronocort formulations in adrenal insufficiency and con…
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CLINICAL_TRIALS trial_result · 2017-01-12Clinical Trial Update: An Open Label Study in Healthy Volunteers to Compare Chronocort® to Hydrocortisone [Phase 1]
Open-label Phase 1 study in healthy volunteers comparing Chronocort (modified-release hydrocortisone) to hydrocortisone.
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CLINICAL_TRIALS research · 2016-12-21Clinical Trial Update: Continuous Subcutaneous Hydrocortisone Infusion in Congenital Adrenal Hyperplasia [Phase 2]
An update on a Phase 2 clinical trial evaluating continuous subcutaneous hydrocortisone infusion for congenital adrenal hyperplasia. The sni…
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CLINICAL_TRIALS research · 2016-09-29Clinical Trial Update: Adrenocortical Functions in Women With Nonclassical 21-hydroxylase Deficiency. [NA]
An update on a clinical trial evaluating adrenocortical function in women with nonclassical 21-hydroxylase deficiency, a form of congenital …
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CLINICAL_TRIALS trial_result · 2016-06-17Clinical Trial Update: Cardiovascular Risk Profile in Patients With Congenital Adrenal Hyperplasia
This clinical trial update reports completion of a study assessing cardiovascular risk in patients with congenital adrenal hyperplasia.
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CLINICAL_TRIALS trial_result · 2015-12-14Clinical Trial Update: Examining Genetic Differences Among People With 21-Hydroxylase Deficiency [NA]
A completed clinical trial update examining genetic differences among individuals with congenital adrenal hyperplasia due to 21-hydroxylase …
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CLINICAL_TRIALS research · 2015-09-17Clinical Trial Update: COrticosteroid in Congenital Adrenal Hyperplasia [Phase 2, Phase 3]
A clinical trial update for a corticosteroid therapy being evaluated in congenital adrenal hyperplasia, spanning Phase 2 and Phase 3. The cu…
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CLINICAL_TRIALS trial_result · 2015-09-14Clinical Trial Update: Research Study for Children With Salt Wasting Congenital Adrenal Hyperplasia [NA]
Clinical trial update for a pediatric study of salt-wasting congenital adrenal hyperplasia (NCT00529841) sponsored by Baylor College of Medi…
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CLINICAL_TRIALS withdrawal · 2015-06-11Clinical Trial Update: Safety, Pharmacokinetics and Pharmacodynamics of NBI-77860 in Adolescent Females With Congenital Adrenal Hyperplasia [Phase 1]
Phase 1 trial evaluating NBI-77860 for congenital adrenal hyperplasia in adolescent females has been withdrawn; the update references safety…
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CLINICAL_TRIALS trial_result · 2014-08-27Clinical Trial Update: Comparison of Two Forms of Hydrocortisone in Patients With Congenital Adrenal Hyperplasia [Phase 1, Phase 2]
A completed clinical trial comparing two forms of hydrocortisone in patients with congenital adrenal hyperplasia due to 21-hydroxylase defic…
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CLINICAL_TRIALS trial_result · 2014-02-28Clinical Trial Update: A Study Examining Doses of Abiraterone Acetate in Adult Women With 21-Hydroxylase Deficiency [Phase 1]
A Phase 1 study evaluated multiple doses of abiraterone acetate in adult women with 21-hydroxylase deficiency (congenital adrenal hyperplasi…
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CLINICAL_TRIALS withdrawal · 2013-09-05Clinical Trial Update: Gene Polymorphisms Influencing Steroid Synthesis and Action
A clinical trial investigating how gene polymorphisms influence steroid synthesis and action has been withdrawn.
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CLINICAL_TRIALS research · 2012-08-17Clinical Trial Update: Clinical Evaluation of NeoPlex4 Assay and NeoPlex System
This update notes the completed clinical evaluation of Luminex's NeoPlex4 Assay and NeoPlex System, assessing tests for congenital adrenal h…
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CLINICAL_TRIALS trial_result · 2011-02-23Clinical Trial Update: Dexamethasone Treatment of Congenital Adrenal Hyperplasia [Phase 2]
A Phase 2 clinical trial studying dexamethasone treatment for congenital adrenal hyperplasia has completed, with results posted.
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CLINICAL_TRIALS research · 2009-11-09Clinical Trial Update: Qualitative Research on Women With Congenital Adrenal Hyperplasia
Completed clinical trial reporting qualitative research findings on women with congenital adrenal hyperplasia.
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CLINICAL_TRIALS research · 2009-06-02Clinical Trial Update: Role of the Protein Osteoprotegerin in the Bone Health of Women With Congenital Adrenal Hyperplasia
A clinical trial update exploring the role of osteoprotegerin in bone health among women with congenital adrenal hyperplasia.
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CLINICAL_TRIALS research · 2008-12-09Clinical Trial Update: Determining the Long-Term Effects of Prenatal Dexamethasone Treatment in Children With 21-Hydroxylase Deficiency and Their Mothers
This clinical trial update focuses on the long-term effects of treating fetuses at risk for 21-hydroxylase congenital adrenal hyperplasia wi…