Cln3 Disease
📧 Sign up to get email alerts when something new happens for Cln3 Disease.
Sign up freeTop drugs studied for this disease
-
CLINICAL_TRIALS trial_result · 2025-09-09Clinical Trial Update: An Open-label Safety, Pharmacokinetic, and Efficacy Study of Miglustat for the Treatment of Subjects With Batten Ceroid Lipofuscinosis, Neuronal 3 (CLN3) Disease [Phase 1, Phase 2]
Open-label Phase 1/2 study evaluating the safety, pharmacokinetics, and efficacy of miglustat in Batten disease due to CLN3; the trial has c…
-
CLINICAL_TRIALS trial_result · 2024-10-23Clinical Trial Update: Optic-to-Audio Device in a Pediatric Cohort With CLN3-related Conditions or Low Vision [NA]
Clinical trial results for an optic-to-audio device tested in pediatric patients with CLN3-related disorders or non-CLN3-related low vision;…