Cln2 Disease
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CLINICAL_TRIALS research · 2025-10-24Clinical Trial Update: Examining Developmental Outcomes of Children Diagnosed With CLN2 Disease
This update indicates an ongoing study evaluating developmental outcomes in children diagnosed with CLN2 disease (Batten disease), currently…
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CLINICAL_TRIALS research · 2025-09-12Clinical Trial Update: ScreenPlus: A Comprehensive, Flexible, Multi-disorder Newborn Screening Program
This clinical trial update describes ScreenPlus, a comprehensive, multi-disorder newborn screening program that is currently enrolling by in…