Citrullinemia
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Sign up freeTop drugs studied for this disease
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CLINICAL_TRIALS trial_result · 2016-02-08Clinical Trial Update: Human Heterologous Liver Cells for Infusion in Children With Urea Cycle Disorders [Phase 2]
Phase 2 trial evaluating infusion of human heterologous liver cells in children with urea cycle disorders has been completed.
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CLINICAL_TRIALS trial_result · 2015-03-20Clinical Trial Update: Nitric Oxide Flux and Ureagenesis in Argininosuccinate Synthetase Deficiency (ASSD)(Citrullinemia I) [NA]
A completed clinical trial investigating nitric oxide flux and ureagenesis in argininosuccinate synthetase deficiency (Citrullinemia I), spo…