Cerebrotendinous Xanthomatosis

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EMA approval · 2025-08-13
EMA Authorised: Chenodeoxycholic acid Leadiant (previously Chenodeoxycholic acid sigma-tau) (chenodeoxycholic acid) — Leadiant GmbH
The EMA authorised Chenodeoxycholic acid Leadiant for Cerebrotedinous xanthomatosis (a rare inborn error of metabolism) with orphan designat…