Cerebellar Ataxia Neuropathy and Vestibular Areflexia Syndrome
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CLINICAL_TRIALS research · 2025-09-05Clinical Trial Update: Pathogenic Insights and Search for Biomarkers in RFC1-ataxia/CANVAS [NA]
An ongoing clinical trial investigating pathogenic insights and biomarker discovery in CANVAS syndrome (RFC1-ataxia) is currently recruiting…