Cdkl5 Deficiency Disorder
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Sign up freeTop drugs studied for this disease
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CLINICAL_TRIALS trial_result · 2026-04-29Clinical Trial Update: A Phase 3 Study to Examine the Efficacy and Safety of ZX008 in Subjects With CDKL5 Deficiency Disorder. [Phase 3]
Phase 3 trial investigating ZX008 for CDKL5 Deficiency Disorder, evaluating efficacy and safety in subjects with CDKL5 Deficiency Disorder a…
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CLINICAL_TRIALS research · 2026-04-21Clinical Trial Update: International CDKL5 Registry
The International CDKL5 Registry trial (NCT04486768) is currently suspended, according to ClinicalTrials.gov.
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CLINICAL_TRIALS trial_result · 2026-04-15Clinical Trial Update: Efficacy and Safety Evaluation of Hyperthermic Baths in the Treatment of Seizures in CDKL5 Deficiency Disorder [NA]
Completed clinical trial evaluating the efficacy and safety of hyperthermic baths for seizures in CDKL5 deficiency disorder. The study was s…
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CLINICAL_TRIALS research · 2026-04-14Clinical Trial Update: The Association Between Fever and CDKL5 Deficiency Disorder: a Nationwide Survey
A nationwide survey investigating the association between fever and CDKL5 Deficiency Disorder has been completed.
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CLINICAL_TRIALS research · 2026-01-05Clinical Trial Update: A Study to Investigate the Efficacy and Safety of ZX008 in Subjects With CDKL5 Deficiency Disorder [Phase 3]
Phase 3 study evaluating ZX008 for CDKL5 deficiency disorder; current status is ACTIVE_NOT_RECRUITING.
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CLINICAL_TRIALS research · 2025-11-28Clinical Trial Update: Double-blind, Randomized, Placebo-controlled Trial of Ganaxolone in CDKL5 Deficiency Patients 6 Months to Less Than 2 Years Old [Phase 3]
A Phase 3, double-blind, randomized, placebo-controlled trial of ganaxolone in children aged 6 months to under 2 years with CDKL5 deficiency…
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CLINICAL_TRIALS research · 2025-03-10Clinical Trial Update: Observational Study in Patients With Cyclin-dependent Kinase-like 5 Deficiency Disorder
This update notes an observational study in patients with CDKL5 deficiency disorder sponsored by the Loulou Foundation, currently active but…
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CLINICAL_TRIALS research · 2024-06-07Clinical Trial Update: Targeting the Gut to Improve Seizure Control in CDKL5 Deficiency Disorder (CDD) [NA]
A University of Milan-sponsored clinical trial for CDKL5 deficiency disorder is currently recruiting to evaluate a gut-targeted strategy aim…
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CLINICAL_TRIALS trial_result · 2023-10-04Clinical Trial Update: Fenfluramine in CDKL5 Deficiency Disorder (CDD) [Phase 2]
Phase 2 trial update for fenfluramine in CDKL5 deficiency disorder has completed with results posted.
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CLINICAL_TRIALS trial_result · 2023-02-16Clinical Trial Update: Ataluren for Nonsense Mutation in CDKL5 and Dravet Syndrome [Phase 2]
Phase 2 trial update for ataluren in nonsense mutation-related CDKL5 and Dravet syndrome (epilepsy) has completed with results posted.
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CLINICAL_TRIALS trial_result · 2022-07-26Clinical Trial Update: Study of Adjunctive Ganaxolone Treatment in Children and Young Adults With CDKL5 Deficiency Disorder [Phase 3]
Phase 3 trial evaluating adjunctive ganaxolone in children and young adults with CDKL5 deficiency disorder has been completed with results p…
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FDA approval · 2022-03-18FDA Approved: ZTALMY — Original Application (Immedica Pharma US Inc)
The FDA approved ZTALMY (ganaxolone) from Immedica Pharma US Inc as an original new drug application for the treatment of seizures associate…
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CLINICAL_TRIALS trial_result · 2021-04-20Clinical Trial Update: A Multicenter, Open-label, Pilot Study of Soticlestat (TAK-935/OV935) in Participants With 15Q Duplication Syndrome (Dup 15q) or Cyclin-Dependent Kinase-Like 5 (CDKL5) Deficiency Disorder (ARCADE STUDY) [Phase 2]
Phase 2 open-label pilot study of soticlestat in Duplication 15q and CDKL5 deficiency disorder has completed with posted results.