Carnitine Palmitoyltransferase Ii Deficiency
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Sign up freeTop drugs studied for this disease
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CLINICAL_TRIALS trial_result · 2021-12-08Clinical Trial Update: Long-Chain Fatty Acid Oxidation Disorders (LC-FAOD) Extension Study for Subjects Previously Enrolled in Triheptanoin Studies [Phase 2]
A Phase 2 extension study update for subjects previously enrolled in triheptanoin studies in long-chain fatty acid oxidation disorders, with…
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CLINICAL_TRIALS trial_result · 2017-03-23Clinical Trial Update: Study of Triheptanoin for Treatment of Long-Chain Fatty Acid Oxidation Disorder [Phase 2]
Phase 2 clinical trial update on triheptanoin for long-chain fatty acid oxidation disorders with results posted in 2017.
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CLINICAL_TRIALS trial_result · 2012-05-30Clinical Trial Update: Effect of Bezafibrate on Muscle Metabolism in Patients With Fatty Acid Oxidation Defects [Phase 2]
Phase 2 trial evaluating bezafibrate’s effect on muscle metabolism in patients with fatty acid oxidation defects; the study status is comple…
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CLINICAL_TRIALS research · 2007-04-09Clinical Trial Update: Bezafibrate Trial in CPT2 Deficiency [Phase 3]
A Phase 3 clinical trial of bezafibrate for Carnitine palmitoyltransferase II deficiency is mentioned, but the current status is unknown.