Carnitine Palmitoyltransferase Deficiency
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CLINICAL_TRIALS trial_result · 2021-12-08Clinical Trial Update: Long-Chain Fatty Acid Oxidation Disorders (LC-FAOD) Extension Study for Subjects Previously Enrolled in Triheptanoin Studies [Phase 2]
A Phase 2 extension study update for subjects previously enrolled in triheptanoin studies in long-chain fatty acid oxidation disorders, with…
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CLINICAL_TRIALS trial_result · 2021-02-11Clinical Trial Update: A Study of UX007 (Triheptanoin) in Participants With Long-Chain Fatty Acid Oxidation Disorders (LC-FAOD) [Phase 2]
Phase 2 clinical trial evaluating UX007 (triheptanoin) in participants with long-chain fatty acid oxidation disorders (LC-FAOD) has complete…
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CLINICAL_TRIALS trial_result · 2010-02-25Clinical Trial Update: Metabolic Consequences of CPT-1 Deficiency [NA]
Clinical trial investigating the metabolic consequences of CPT-1A deficiency has completed.