Carbamoyl-phosphate Synthase Deficiency Disease
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Sign up freeTop drugs studied for this disease
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EMA approval · 2026-08-17EMA Authorised: Pheburane (sodium phenylbutyrate) — Eurocept International B. V.
EMA authorised Pheburane (sodium phenylbutyrate) for Carbamoyl-Phosphate Synthase I Deficiency disease, under Eurocept International B.V.
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EMA approval · 2022-12-16EMA Authorised: Ammonaps (sodium phenylbutyrate) — Immedica Pharma AB
EMA authorised Ammonaps (sodium phenylbutyrate) for OTCD, citrullinemia, and CPS1 deficiency conditions.