Bone Marrow Failure
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Sign up freeTop drugs studied for this disease
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CLINICAL_TRIALS research · 2026-02-06Clinical Trial Update: Study to Evaluate of EXG34217 in Patients With Telomere Biology Disorders With Bone Marrow Failure [Phase 1]
Clinical trial update announcing a Phase 1 study of EXG34217 in patients with telomere biology disorders and bone marrow failure, currently …
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CLINICAL_TRIALS research · 2026-01-30Clinical Trial Update: Alpha/Beta TCD HCT in Patients With Inherited BMF Disorders [Phase 2]
Phase 2 clinical trial update investigating alpha/beta T cell receptor alpha/beta-depleted hematopoietic cell transplantation in inherited b…
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CLINICAL_TRIALS research · 2026-01-29Clinical Trial Update: The HOPE Biobank Resource (BMT CTN 2402 HOPE)
This update announces the HOPE Biobank Resource for BMT CTN 2402, which is currently not yet recruiting and will support research in aplasti…
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CLINICAL_TRIALS research · 2025-12-22Clinical Trial Update: Molecular and Clinical Analysis of Bone Marrow Failure: A Secondary Research Study
A clinical trial update describing a secondary research study that analyzes molecular and clinical aspects of bone marrow failure and VEXAS …
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CLINICAL_TRIALS research · 2025-11-28Clinical Trial Update: Regenerative Medicine to Restore Hematopoiesis and Immune Function in Immunodeficiencies and Inherited Bone Marrow Failures [Phase 2]
Phase 2 clinical trial update on regenerative medicine to restore hematopoiesis and immune function in immunodeficiencies and inherited bone…
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CLINICAL_TRIALS research · 2025-08-14Clinical Trial Update: CD34+ (Non-Malignant) Stem Cell Selection for Patients Receiving Allogeneic Stem Cell Transplantation [Phase 1, Phase 2]
This document provides an update on a phase 1/2 clinical trial evaluating CD34+ stem cell selection for patients receiving allogeneic stem c…
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CLINICAL_TRIALS research · 2025-05-22Clinical Trial Update: Expanded Access Protocol Using Alpha/Beta T and CD19+ Depleted PBSC
This clinical trial update describes an expanded access protocol using alpha/beta T and CD19+ depleted peripheral blood stem cells. It targe…
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CLINICAL_TRIALS research · 2024-12-31Clinical Trial Update: Avatrombopag for Platelet Recovery Post-UCBT in Patients With Bone Marrow Failure Disease
This clinical trial is recruiting to evaluate avatrombopag for promoting platelet recovery after umbilical cord blood transplantation in pat…