Bone Marrow Failure Syndrome
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Sign up freeTop drugs studied for this disease
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CLINICAL_TRIALS research · 2025-07-04Clinical Trial Update: Haploidentical HCT for Severe Aplastic Anemia [Phase 2]
This document provides an update on a Phase 2 clinical trial evaluating haploidentical hematopoietic cell transplantation for severe aplasti…
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CLINICAL_TRIALS research · 2025-06-24Clinical Trial Update: TCR Alpha Beta T-cell Depleted Haploidentical HCT in the Treatment of Non-Malignant Hematological Disorders in Children [Phase 2]
A Phase 2 clinical trial at Johns Hopkins All Children's Hospital is evaluating TCR alpha-beta T-cell-depleted haploidentical hematopoietic …
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CLINICAL_TRIALS research · 2025-01-22Clinical Trial Update: CD7 CAR-T Cell Sequential Allo-HSCT for Non-malignant Blood and Immune System Diseases [EARLY_Phase 1]
Phase 1 study evaluating CD7 CAR-T cell therapy sequentially with allogeneic HSCT for bone marrow failure syndrome, a non-malignant blood an…
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CLINICAL_TRIALS trial_result · 2023-09-15Clinical Trial Update: Conditioning Regimen for Allogeneic Hematopoietic Stem-Cell Transplantation [Phase 1, Phase 2]
A Phase 1/2 clinical trial evaluating conditioning regimens for allogeneic hematopoietic stem-cell transplantation has completed recruitment…
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CLINICAL_TRIALS trial_result · 2020-02-26Clinical Trial Update: Pilot Trial of Clofarabine Added to Standard Busulfan and Fludarabine for Conditioning Prior to Allogeneic Hematopoietic Cell Transplantation [Phase 2]
A Phase 2 pilot trial evaluating adding clofarabine to standard busulfan/fludarabine conditioning for allogeneic hematopoietic cell transpla…
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CLINICAL_TRIALS trial_result · 2016-04-22Clinical Trial Update: Memory T-cell Infusion to Improve Immunity After TCR-alpha/Beta Depleted Hematopoietic Stem Cell Transplantation [Phase 1, Phase 2]
Clinical trial update on memory T-cell infusion after TCR-alpha/beta depleted hematopoietic stem cell transplantation, with Phase 1/2 status…
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CLINICAL_TRIALS research · 2015-12-22Clinical Trial Update: The Impact of Red Cell Age on Product Utilization in the Chronically Transfused Outpatient Population [Phase 3]
Phase 3 clinical trial update examining how red cell age influences product utilization in chronically transfused outpatients with bone marr…
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CLINICAL_TRIALS trial_result · 2015-06-19Clinical Trial Update: Eltrombopag for Enhancing Platelet Engraftment in Adult Patients Undergoing Cord Blood Transplantation [Phase 2]
Phase 2 trial update on eltrombopag to enhance platelet engraftment in adult cord blood transplantation. The conditions include hematologic …
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CLINICAL_TRIALS trial_result · 2014-08-13Clinical Trial Update: Reduced Intensity Conditioning for Umbilical Cord Blood Transplant in Pediatric Patients With Non-Malignant Disorders [Phase 1]
Clinical trial update on reduced intensity conditioning for umbilical cord blood transplantation in pediatric patients with non-malignant di…