Biallelic Rpe65 Mutation-associated Retinal Dystrophy
📧 Sign up to get email alerts when something new happens for Biallelic Rpe65 Mutation-associated Retinal Dystrophy.
Sign up freeTop drugs studied for this disease
-
CLINICAL_TRIALS trial_result · 2026-06-04Clinical Trial Update: Study of Efficacy and Safety of Voretigene Neparvovec in Japanese Patients With Biallelic RPE65 Mutation-associated Retinal Dystrophy [Phase 3]
A Phase 3 trial evaluating the efficacy and safety of voretigene neparvovec in Japanese patients with biallelic RPE65 mutation-associated re…