Beta-thalassemia
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Sign up freeTop drugs studied for this disease
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CLINICAL_TRIALS research · 2025-08-12Clinical Trial Update: A Study to Evaluate Luspatercept (ACE-536) in Chinese Participants Who Require Regular Red Blood Cell Transfusions Due to Beta (β)-Thalassemia. [Phase 2]
This is a Phase 2 clinical trial evaluating luspatercept (ACE-536) in Chinese participants with beta-thalassemia who require regular red blo…
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CLINICAL_TRIALS research · 2025-08-08Clinical Trial Update: AlloSCT for Malignant and Non-malignant Hematologic Diseases Utilizing Alpha/Beta T Cell and CD19+ B Cell Depletion [Phase 2]
A Phase 2 clinical trial evaluating allogeneic stem cell transplantation with alpha/beta T cell and CD19+ B cell depletion for malignant and…
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CLINICAL_TRIALS research · 2025-08-05Clinical Trial Update: Safety and Efficacy of the Lentiviral Vector in Gene Therapy of Beta-thalassemia Patients [NA]
The document discusses a lentiviral vector gene therapy being evaluated for beta-thalassemia. The trial is currently recruiting.
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CLINICAL_TRIALS research · 2025-03-10Clinical Trial Update: Β-Thalassemia Treatment with KL003 Cell Injection [Phase 1, Phase 2]
A Phase 1/2 clinical trial evaluating KL003 cell injection for transfusion-dependent beta-thalassemia is currently recruiting.
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CLINICAL_TRIALS research · 2025-02-18Clinical Trial Update: ERN-EuroBloodNet Registry on Patients With Rare Red Blood Cell Defects and COVID-19
This clinical trials registry update reports completion of the ERN-EuroBloodNet registry documenting patients with rare red blood cell defec…
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CLINICAL_TRIALS research · 2025-01-14Clinical Trial Update: A Multiple Ascending Dose Study of 9MW3011 in Patients With Non-transfusion-dependent β-thalassemia [Phase 1]
A Phase 1 multiple ascending dose study of 9MW3011 in patients with beta-thalassemia is currently recruiting.
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CLINICAL_TRIALS research · 2024-11-29Clinical Trial Update: the Safety and Efficacy Evaluation of HGI-001 Injection in Patients With Transfusion-Dependent β-Thalassemia [EARLY_Phase 1]
This document reports an early-phase 1 clinical trial evaluating the safety and efficacy of HGI-001 Injection in transfusion-dependent beta-…
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CLINICAL_TRIALS research · 2024-11-29Clinical Trial Update: Safety and Efficacy Evaluation of β-globin Restored Autologous Hematopoietic Stem Cells in β-thalassemia Major Patients [EARLY_Phase 1]
Early-phase clinical trial update evaluating safety and efficacy of β-globin–restored autologous hematopoietic stem cells in β-thalassemia m…
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CLINICAL_TRIALS research · 2024-11-14Clinical Trial Update: FLOWER: Following Longitudinal Outcomes With Epidemiology for Rare Diseases
FLOWER is a longitudinal epidemiology study by xCures to follow outcomes across multiple rare diseases, and the study is currently recruitin…
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CLINICAL_TRIALS research · 2024-11-06Clinical Trial Update: A Post-Marketing Surveillance Study to Assess Safety of Luspatercept in Korean Patients With Myelodysplastic Syndrome or β-thalassemia
A post-marketing surveillance study to assess the safety of luspatercept in Korean patients with myelodysplastic syndrome or beta-thalassemi…
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CLINICAL_TRIALS research · 2024-10-23Clinical Trial Update: Evaluating Safety and Efficacy of Lentiviral-transduced CD34+ HSCs in Β-thalassaemia Patients. [Phase 1]
Phase 1 clinical trial evaluating safety and efficacy of lentiviral-transduced CD34+ hematopoietic stem cells in beta-thalassemia patients; …
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CLINICAL_TRIALS research · 2024-08-23Clinical Trial Update: Adherence of Beta Thalssemia Patients to Oral Chelation Therapy [NA]
This clinical trial update indicates Sohag University is recruiting Beta-thalassemia patients to study adherence to oral chelation therapy.
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CLINICAL_TRIALS research · 2024-06-04Clinical Trial Update: EKLF Gene Expression in β-thalassemia
A clinical trial investigating EKLF gene expression in beta-thalassemia; the study is currently not yet recruiting.
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CLINICAL_TRIALS research · 2024-05-29Clinical Trial Update: Detection of Krupple Like Factor -1(KLF1/ EKLF) DNA Mutations in Beta Thalassemia Patients
This clinical trial update outlines a study to detect KLF1/EKLF DNA mutations in beta-thalassemia patients. The trial status is NOT_YET_RECR…
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CLINICAL_TRIALS research · 2024-05-13Clinical Trial Update: Thyroid Function , HbA1c in Relation to Ferritin Level in Adullt Patient e B Thalassemia
A clinical trial update describing a study on thyroid function and HbA1c in relation to ferritin levels in adult patients with beta-thalasse…
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CLINICAL_TRIALS research · 2024-05-07Clinical Trial Update: Thrombophilia In Beta Thalassemia
This clinical trial update notes a study investigating thrombophilia in patients with beta-thalassemia. The trial is not yet recruiting.
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CLINICAL_TRIALS research · 2019-01-30Clinical Trial Update: Detection Of β-thalassemia Carriers In Assiut [NA]
This clinical trial update from Assiut University concerns detection of beta-thalassemia carriers in Assiut. The status is unknown and no tr…
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CLINICAL_TRIALS research · 2018-07-19Clinical Trial Update: The Use of CGMS to Detect Alterations of Blood Glucose in Thalassemic Patients [NA]
A completed clinical trial update examining the use of continuous glucose monitoring to detect blood glucose changes in patients with beta-t…
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CLINICAL_TRIALS research · 2017-11-30Clinical Trial Update: Quality of Life and Treatment Satisfaction in β-Thalassemia Patients Receiving Deferasirox
An update on a clinical trial evaluating quality of life and treatment satisfaction in beta-thalassemia patients treated with deferasirox.
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CLINICAL_TRIALS research · 2010-03-24Clinical Trial Update: Prevalence Of Microalbuminuria Among Children Suffering From Sickle Cell Nephropathy and Sickle Cell/Beta-Thalassemia
A clinical trial update assessing how common microalbuminuria is among children with sickle cell nephropathy and sickle cell/beta-thalassemi…