CLINICAL_TRIALS
research
· 2025-08-05
Clinical Trial Update: Safety and Efficacy of the Lentiviral Vector in Gene Therapy of Beta-thalassemia Patients [NA]
Summary
The document discusses a lentiviral vector gene therapy being evaluated for beta-thalassemia. The trial is currently recruiting.
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Diseases / indications
Drugs mentioned
Snippet
Sponsor: Institute of Hematology & Blood Diseases Hospital, China | Conditions: Transfusion-dependent Beta-Thalassemia | NA | Status: RECRUITING