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CLINICAL_TRIALS research · 2025-08-05

Clinical Trial Update: Safety and Efficacy of the Lentiviral Vector in Gene Therapy of Beta-thalassemia Patients [NA]

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Summary

The document discusses a lentiviral vector gene therapy being evaluated for beta-thalassemia. The trial is currently recruiting.

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Diseases / indications

Drugs mentioned

  • Lentiviral vector gene therapy for beta-thalassemia

Snippet

Sponsor: Institute of Hematology & Blood Diseases Hospital, China | Conditions: Transfusion-dependent Beta-Thalassemia | NA | Status: RECRUITING