Beta Thalassemia Major
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Sign up freeTop drugs studied for this disease
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CLINICAL_TRIALS trial_result · 2018-07-18Clinical Trial Update: The Potential Hepatoprotective Effect of Metformin in Patients With Beta Thalassemia Major [Phase 4]
This document covers a Phase 4 clinical trial evaluating whether metformin has hepatoprotective effects in patients with beta-thalassemia ma…
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CLINICAL_TRIALS trial_result · 2018-07-12Clinical Trial Update: Effect of Spirulina Compared to Amlodipine on Cardiac Iron Overload in Children With Beta Thalassemia [NA]
A completed clinical trial compared spirulina supplementation to amlodipine for cardiac iron overload in children with beta-thalassemia majo…
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FDA approval · 2018-05-11FDA Approved: JADENU — Supplemental Application (Novartis Pharmaceuticals Corporation)
FDA approved a supplemental application for JADENU (deferasirox) from Novartis Pharmaceuticals Corporation, expanding its labeling for iron …
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FDA approval · 2018-04-20FDA Approved: FERRIPROX — Supplemental Application (Chiesi USA, Inc.)
The FDA approved a supplemental application for Ferriprox (deferiprone) filed by Chiesi USA, Inc., resulting in updated labeling for iron ch…
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CLINICAL_TRIALS trial_result · 2017-10-25Clinical Trial Update: the Potential Immunomodulatory Effects of Spirulina on Thalassemic Children [NA]
A completed clinical trial evaluated the potential immunomodulatory effects of Spirulina in children with beta-thalassemia major.
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CLINICAL_TRIALS trial_result · 2017-10-20Clinical Trial Update: Reduced Intensity Transplant Conditioning Regimen for Severe Thalassemia [Phase 2]
Phase 2 trial evaluating a reduced-intensity transplant conditioning regimen for severe thalassemia has completed, with results posted in Oc…
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CLINICAL_TRIALS trial_result · 2017-09-08Clinical Trial Update: Gene Therapy for Beta-Thalassemia Major Using Autologous Hematopoietic Stem Cell Genetically Modified [Phase 1, Phase 2]
Clinical trial update for autologous gene therapy for beta-thalassemia major in Phase 1/2.
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FDA approval · 2017-05-18FDA Approved: JADENU — Original Application (Novartis Pharmaceuticals Corporation)
The FDA approved Jadenu (deferasirox) from Novartis as an oral iron chelator for chronic iron overload due to blood transfusions. This is th…
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CLINICAL_TRIALS research · 2017-04-26Clinical Trial Update: Benefits of Nigella Sativa in Children With Beta Thalassemia Major [EARLY_Phase 1]
An early-phase 1 clinical trial investigating Nigella Sativa for children with beta-thalassemia major, with the trial status not specified.
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CLINICAL_TRIALS research · 2017-04-25Clinical Trial Update: Study of The Therapeutic Benefits of Al-hijamah in Children With Beta Thalassemia Major [NA]
A clinical trial update evaluating Al-hijamah as a treatment for beta-thalassemia major in children; the current status is unknown.
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CLINICAL_TRIALS withdrawal · 2017-04-20Clinical Trial Update: An Open Label Study to Evaluate the Pharmacokinetics, Safety, Tolerability and Efficacy of Deferasirox Administered to Chinese Patients With β-thalassemia Major Aged From 2 to Less Than 6 Years Old [Phase 4]
An open-label Phase 4 trial evaluating deferasirox in Chinese children aged 2 to less than 6 with beta-thalassemia major has been withdrawn.
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CLINICAL_TRIALS research · 2017-01-09Clinical Trial Update: Sperm DNA Damage in β-thalassemia Major: Is There a Role for Antioxidants? [Phase 1, Phase 2]
This clinical trial update investigates whether antioxidants can mitigate sperm DNA damage in men with beta-thalassemia major, spanning Phas…
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CLINICAL_TRIALS trial_result · 2016-11-25Clinical Trial Update: Assess the Feasibility and Safety of Granulocyte Colony Stimulating Factor (GCSF) Mobilization of CD34+ Hematopoietic Progenitor Cells in Patients With Betathalassemia Major [NA]
This completed clinical trial evaluated the feasibility and safety of mobilizing CD34+ hematopoietic progenitor cells using granulocyte colo…
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CLINICAL_TRIALS trial_result · 2016-07-21Clinical Trial Update: Post Hematopoietic Stem Cell Transplantation [Phase 4]
Novartis-sponsored Phase 4 trial evaluating iron overload after hematopoietic stem cell transplantation in patients with beta-thalassemia ma…
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CLINICAL_TRIALS research · 2015-04-16Clinical Trial Update: Unrelated Umbilical Cord Blood Following HLA-haploidentical Hematopoietic Stem Cell Transplantation in Patients With β-thalassemia Major [NA]
ClinicalTrials.gov entry describes a study using unrelated umbilical cord blood after haploidentical hematopoietic stem cell transplantation…
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CLINICAL_TRIALS research · 2015-01-14Clinical Trial Update: An Algorithm to Start Iron Chelation in Minimally Transfused Young Beta-thalassemia Major Patients [Phase 2, Phase 3]
A clinical trial update describing a Phase 2/Phase 3 study evaluating an algorithm to start iron chelation in minimally transfused young pat…
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CLINICAL_TRIALS trial_result · 2014-08-29Clinical Trial Update: Beta-thalassemia and Microparticles [NA]
Completed clinical trial update investigating beta-thalassemia (major and intermedia) and microparticles.
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CLINICAL_TRIALS trial_result · 2014-07-23Clinical Trial Update: Clinical Trial of Deferasirox Combination Treatment With Deferiprone In Thalassaemia Patients [NA]
Completed clinical trial evaluating the combination of deferasirox and deferiprone in patients with beta-thalassemia major.
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CLINICAL_TRIALS trial_result · 2014-03-04Clinical Trial Update: Thalassemia (Cooley's Anemia) Clinical Research Network (TCRN)
The Thalassemia Clinical Research Network trial has completed its study (status COMPLETED) under sponsor Carelon Research.
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CLINICAL_TRIALS research · 2013-05-06Clinical Trial Update: B Memory Cell Response to Vaccination With the 13-valent Pneumococcal Conjugate Vaccine in Asplenic Individuals [Phase 4]
This clinical trial update describes a Phase 4 study evaluating B memory cell responses to the 13-valent pneumococcal conjugate vaccine in i…
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CLINICAL_TRIALS trial_result · 2012-12-20Clinical Trial Update: Evaluating the Safety of G-CSF Mobilization in Individuals With Beta Thalassemia Major [NA]
This completed clinical trial evaluated the safety of granulocyte colony-stimulating factor (G-CSF) mobilization in individuals with beta-th…
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CLINICAL_TRIALS trial_result · 2012-12-19Clinical Trial Update: Immunomodulatory Effects of Silymarin in Patients With Beta-Thalassemia Major [Phase 1]
Phase 1 clinical trial evaluating the immunomodulatory effects of silymarin in patients with beta-thalassemia major. The study status is com…
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FDA approval · 2012-11-15FDA Approved: FERRIPROX — Supplemental Application (Chiesi USA, Inc.)
The FDA approved a supplemental application for Ferriprox (deferiprone) filed by Chiesi USA, Inc., to modify/expand the product’s labeling.
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CLINICAL_TRIALS approval · 2012-02-09Clinical Trial Update: Compassionate Use of Deferiprone for Patients With Thalassemia and Iron-Induced Heart Disease
Deferiprone has received approval for marketing to treat iron overload in patients with thalassemia and iron-induced heart disease.
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CLINICAL_TRIALS research · 2012-02-06Clinical Trial Update: Study Of Efficacy,Safety of Combined Deferasirox and Deferiprone Versus Combined Deferiprone and Desferal In Conditions of Iron Overload [Phase 2, Phase 3]
A Phase 2/3 clinical trial comparing the combination of deferasirox and deferiprone to the combination of deferiprone and deferoxamine (Desf…