Bardet-biedl Syndrome Type

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CLINICAL_TRIALS trial_result · 2026-03-31
Clinical Trial Update: First-in-Human, Dose Escalation Trial of AXV-101 in BBS1-Related Retinal Degeneration [EARLY_Phase 1]
This notice reports a first-in-human, dose-escalation Phase 1 trial of AXV-101 for Bardet-Biedl syndrome type 1–related retinal degeneration…