Autosomal Recessive Hypophosphatemic Rickets
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CLINICAL_TRIALS trial_result · 2026-08-10Clinical Trial Update: ENERGY 2: Evaluation of the Efficacy and Safety of INZ-701 in Infants With ENPP1 Deficiency [Phase 3]
Phase 3 clinical trial evaluating INZ-701 for ENPP1 deficiency in infants, focusing on efficacy and safety; status ACTIVE_NOT_RECRUITING.
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CLINICAL_TRIALS research · 2026-03-24Clinical Trial Update: The ENERGY Study: Evaluation of Safety and Tolerability of INZ-701 in Infants With ENPP1 Deficiency or ABCC6 Deficiency [Phase 1]
Phase 1 clinical trial update evaluating the safety and tolerability of INZ-701 in infants with ENPP1 or ABCC6 deficiencies.
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CLINICAL_TRIALS research · 2026-03-18Clinical Trial Update: ENERGY 2: Evaluation of the Efficacy and Safety of INZ-701 in Infants With ENPP1 Deficiency [Phase 3]
This clinical trial update notes that INZ-701 is in Phase 3 trials to evaluate efficacy and safety in infants with ENPP1 deficiency, Autosom…
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CLINICAL_TRIALS research · 2025-05-01Clinical Trial Update: The ENERGY 3 Study: Evaluation of Efficacy and Safety of INZ-701 in Children With ENPP1 Deficiency [Phase 3]
Phase 3 clinical trial evaluating INZ-701 for ENPP1 deficiency in children, with ongoing status (ACTIVE_NOT_RECRUITING).
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CLINICAL_TRIALS withdrawal · 2025-05-01Clinical Trial Update: The ENABLE Study: Safety and Efficacy Study of INZ-701 in Patients With ENPP1 Deficiency [Phase 2]
The Phase 2 ENABLE study evaluating INZ-701 for ENPP1 deficiency and related diseases has been withdrawn.
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CLINICAL_TRIALS trial_result · 2025-02-05Clinical Trial Update: Evaluation of Safety, Tolerability, and Efficacy of INZ-701 in Adults With ENPP1 Deficiency [Phase 1, Phase 2]
This clinical trial update announces completion of Phase 1/2 evaluation of INZ-701 in adults with ENPP1 deficiency, assessing safety, tolera…
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CLINICAL_TRIALS trial_result · 2024-09-19Clinical Trial Update: Natural History Study of ENPP1 Deficiency and the Early-onset Form of ABCC6 Deficiency
Completed natural history study assessing ENPP1 deficiency and early-onset ABCC6 deficiency, including related conditions Generalized Arteri…