Atp-binding Cassette Subfamily Member Deficiency
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CLINICAL_TRIALS trial_result · 2024-09-19Clinical Trial Update: Natural History Study of ENPP1 Deficiency and the Early-onset Form of ABCC6 Deficiency
Completed natural history study assessing ENPP1 deficiency and early-onset ABCC6 deficiency, including related conditions Generalized Arteri…