Aromatic L-amino Acid Decarboxylase Deficiency
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CLINICAL_TRIALS trial_result · 2023-02-10Clinical Trial Update: A Phase I/II Clinical Trial for Treatment of Aromatic L-amino Acid Decarboxylase (AADC) Deficiency Using AAV2-hAADC [Phase 1, Phase 2]
Phase I/II clinical trial evaluating AAV2-hAADC gene therapy for Aromatic L-amino Acid Decarboxylase (AADC) deficiency has completed.
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CLINICAL_TRIALS trial_result · 2017-04-28Clinical Trial Update: Newborn Screening for Aromatic L-amino Acid Decarboxylase Deficiency
A completed clinical trial assessing newborn screening for aromatic L-amino acid decarboxylase deficiency in newborns.