Aromatic Amino Acid Decarboxylase Deficiency

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CLINICAL_TRIALS trial_result · 2023-02-10
Clinical Trial Update: A Clinical Trial for Treatment of Aromatic L-amino Acid Decarboxylase (AADC) Deficiency Using AAV2-hAADC - An Expansion [Phase 2]
Phase 2 expansion study of AAV2-hAADC gene therapy for aromatic amino acid decarboxylase (AADC) deficiency has completed.