Alpha-1 Antitrypsin Deficiency-associated Liver Disease
📧 Sign up to get email alerts when something new happens for Alpha-1 Antitrypsin Deficiency-associated Liver Disease.
Sign up freeTop drugs studied for this disease
-
CLINICAL_TRIALS trial_result · 2025-04-20Clinical Trial Update: Study of Fazirsiran (TAK-999, ARO-AAT) in Patients With Alpha-1 Antitrypsin Deficiency Associated Liver Disease (AATD) [Phase 2]
Phase 2 study of Fazirsiran (TAK-999, ARO-AAT) for Alpha-1 antitrypsin deficiency–associated liver disease has completed with results posted…
-
CLINICAL_TRIALS withdrawal · 2024-09-19Clinical Trial Update: An Extension Study of Belcesiran in Patients With Alpha-1 Antitrypsin Deficiency Associated Liver Disease (AATLD) [Phase 2]
The Phase 2 extension study of belcesiran for Alpha-1 Antitrypsin Deficiency-associated liver disease has been withdrawn. Sponsor: Dicerna P…