Ala Dehydratase Deficiency Porphyria
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CLINICAL_TRIALS trial_result · 2020-02-11Clinical Trial Update: ENVISION: A Study to Evaluate the Efficacy and Safety of Givosiran (ALN-AS1) in Patients With Acute Hepatic Porphyrias (AHP) [Phase 3]
Phase 3 trial evaluating givosiran (ALN-AS1) for acute hepatic porphyrias has been completed with results posted.
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CLINICAL_TRIALS trial_result · 2019-01-25Clinical Trial Update: INSIGHT-AHP: A Study to Characterize the Prevalence of Acute Hepatic Porphyria (AHP) in Patients With Clinical Presentation and History Consistent With AHP
A terminated Alnylam-sponsored study (INSIGHT-AHP) sought to characterize the prevalence of acute hepatic porphyrias among patients with cli…