Ada-scid

• CLINICAL_TRIALS trial_result · 2021-09-20
  Clinical Trial Update: Autologous CD34+ Hematopoietic Stem Cells Transduced ex Vivo With Elongation Factor 1 Alpha Shortened (EFS) Lentiviral Vector Encoding for the Human ADA Gene [Phase 1, Phase 2]

  Phase 1/2 clinical trial assessing autologous CD34+ hematopoietic stem cells transduced with an ADA gene lentiviral vector in ADA-SCID; stud…

• CLINICAL_TRIALS trial_result · 2020-07-31
  Clinical Trial Update: ADA Gene Transfer Into Hematopoietic Stem/Progenitor Cells for the Treatment of ADA-SCID [Phase 2]

  Phase 2 clinical trial of ADA gene transfer into hematopoietic stem/progenitor cells for ADA-SCID has been completed with results posted.

• CLINICAL_TRIALS trial_result · 2020-04-16
  Clinical Trial Update: EZN-2279 in Patients With ADA-SCID [Phase 3]

  Phase 3 trial update for EZN-2279 in ADA-SCID has completed; results posted in 2020.