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Diseases · Acid Sphingomyelinase Deficiency

Acid Sphingomyelinase Deficiency

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Top drugs studied for this disease

XENPOZYME (6)
Olipudase alfa (3)
rhASM Enzyme Replacement Therapy (1)
recombinant human acid sphingomyelinase (1)
GammaGA (1)
Xenpozyme (olipudase alfa) (1)

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Data: openFDA, ClinicalTrials.gov, EMA. Analysis by GPT-5-nano. Not medical advice. · Methodology · Privacy · Terms