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CLINICAL_TRIALS research · 2025-07-23

Clinical Trial Update: Validation of a Questionnaire for Quality of Life Assessment in Patients With Transthyretin Amyloidosis.

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Summary

A clinical trial update describes validation of a quality-of-life questionnaire for patients with transthyretin amyloidosis to support future research and clini…

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Diseases / indications

Snippet

Sponsor: Hospital General de Niños Pedro de Elizalde | Conditions: Amyloidosis in Transthyretin (TTR), Hereditary Amyloidosis, Transthyretin-Related | Status: ACTIVE_NOT_RECRUITING