CLINICAL_TRIALS
research
· 2025-07-23
Clinical Trial Update: Validation of a Questionnaire for Quality of Life Assessment in Patients With Transthyretin Amyloidosis.
Summary
A clinical trial update describes validation of a quality-of-life questionnaire for patients with transthyretin amyloidosis to support future research and clini…
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Diseases / indications
Snippet
Sponsor: Hospital General de Niños Pedro de Elizalde | Conditions: Amyloidosis in Transthyretin (TTR), Hereditary Amyloidosis, Transthyretin-Related | Status: ACTIVE_NOT_RECRUITING