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CLINICAL_TRIALS research · 2025-07-23

Clinical Trial Update: Study on the Safety and Efficacy of RAG-21 in the Treatment of Amyotrophic Lateral Sclerosis Patients With FUS Gene Mutations [EARLY_Phase 1]

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Summary

An early-phase 1 clinical trial update reports evaluating the safety and potential efficacy of RAG-21 for amyotrophic lateral sclerosis in patients with FUS gen…

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Diseases / indications

Drugs mentioned

  • RAG-21

Snippet

Sponsor: Beijing Tiantan Hospital | Conditions: Amyotrophic Lateral Sclerosis (ALS) | EARLY_Phase 1 | Status: NOT_YET_RECRUITING