Catalyst Wire Dossier Catalyst Wire Dossier
CLINICAL_TRIALS trial_result · 2025-07-24

Clinical Trial Update: An Extension Study of JR-141-BR21 in Patients With Mucopolysaccharidosis II [Phase 2]

View source ↗

Summary

Phase 2 extension study update for JR-141-BR21 in patients with Mucopolysaccharidosis II; the study is currently active but not recruiting.

Upgrade for the full analysis, importance score, and drug timeline.

Diseases / indications

Drugs mentioned

  • JR-141-BR21

Snippet

Sponsor: JCR Pharmaceuticals Co., Ltd. | Conditions: Mucopolysaccharidosis II | Phase 2 | Status: ACTIVE_NOT_RECRUITING