Clinical Trial Update: A Multi-cohort Study of Safety, Efficacy, PK and PD of GNR-055 in Patients With Mucopolysaccharidosis Type II [Phase 2, Phase 3]

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Summary

A multi-cohort Phase 2/3 trial is evaluating safety, efficacy, pharmacokinetics and pharmacodynamics of GNR-055 in patients with Mucopolysaccharidosis Type II; …

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Diseases / indications

• Mucopolysaccharidosis Type Ii

Drugs mentioned

• GNR-055 (GNR-055)

Snippet

Sponsor: AO GENERIUM | Conditions: Mucopolysaccharidosis Type II, Metabolic Diseases | Phase 2, Phase 3 | Status: RECRUITING