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CLINICAL_TRIALS trial_result · 2025-07-31

Clinical Trial Update: A Trial to Learn if Receiving ALN-PNP siRNA is Safe and Well Tolerated, and How it Works in Adult Participants With Nonalcoholic Fatty Liver Disease (NAFLD) and a Genetic Risk Factor [Phase 1]

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Summary

Phase 1 clinical trial update assessing safety, tolerability, and mechanism of ALN-PNP siRNA in adults with nonalcoholic fatty liver disease and a genetic risk …

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Diseases / indications

Drugs mentioned

  • ALN-PNP siRNA (ALN-PNP siRNA)

Snippet

Sponsor: Regeneron Pharmaceuticals | Conditions: Nonalcoholic Fatty Liver Disease (NAFLD), Nonalcoholic Steatohepatitis (NASH) | Phase 1 | Status: COMPLETED