CLINICAL_TRIALS
research
· 2025-08-05
Clinical Trial Update: Personalized Antisense Oligonucleotide Therapy for A Single Participant With CHCHD10 ALS [Phase 1, Phase 2]
Summary
A single-participant Phase 1/2 trial is evaluating a personalized antisense oligonucleotide therapy for CHCHD10-related amyotrophic lateral sclerosis. The study…
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Diseases / indications
Drugs mentioned
Snippet
Sponsor: n-Lorem Foundation | Conditions: Amyotrophic Lateral Sclerosis | Phase 1, Phase 2 | Status: ACTIVE_NOT_RECRUITING