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CLINICAL_TRIALS research · 2025-08-07

Clinical Trial Update: Gene Therapy for Children With CLN3 Batten Disease [Phase 1, Phase 2]

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Summary

A Phase 1/2 gene therapy trial for children with CLN3 Batten disease, sponsored by Alcyone Therapeutics, is currently active but not recruiting.

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Diseases / indications

Drugs mentioned

  • ALCYONE CLN3 gene therapy

Snippet

Sponsor: Alcyone Therapeutics, Inc | Conditions: CLN3, Batten Disease | Phase 1, Phase 2 | Status: ACTIVE_NOT_RECRUITING