CLINICAL_TRIALS
research
· 2025-08-07
Clinical Trial Update: Gene Therapy for Children With CLN3 Batten Disease [Phase 1, Phase 2]
Summary
A Phase 1/2 gene therapy trial for children with CLN3 Batten disease, sponsored by Alcyone Therapeutics, is currently active but not recruiting.
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Diseases / indications
Drugs mentioned
Snippet
Sponsor: Alcyone Therapeutics, Inc | Conditions: CLN3, Batten Disease | Phase 1, Phase 2 | Status: ACTIVE_NOT_RECRUITING