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CLINICAL_TRIALS research · 2025-08-13

Clinical Trial Update: Safety, Tolerability, Pharmacodynamic, Efficacy, and Pharmacokinetic Study of DYNE-251 in Participants With Duchenne Muscular Dystrophy Amenable to Exon 51 Skipping [Phase 1, Phase 2]

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Summary

A Phase 1/2 clinical trial update evaluating the safety, tolerability, pharmacodynamics, efficacy, and pharmacokinetics of DYNE-251 in Duchenne muscular dystrop…

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Diseases / indications

Drugs mentioned

  • DYNE-251

Snippet

Sponsor: Dyne Therapeutics | Conditions: Duchenne Muscular Dystrophy (DMD) | Phase 1, Phase 2 | Status: ACTIVE_NOT_RECRUITING