CLINICAL_TRIALS
trial_result
· 2025-08-14
Clinical Trial Update: Ambroxol as a Disease-modifying Treatment in GBA-PD [Phase 2]
Summary
Phase 2 trial evaluating ambroxol as a disease-modifying therapy for Parkinson disease with GBA mutation has completed.
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Diseases / indications
Drugs mentioned
Snippet
Sponsor: Fondazione I.R.C.C.S. Istituto Neurologico Carlo Besta | Conditions: Parkinson Disease, GBA Gene Mutation | Phase 2 | Status: COMPLETED