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CLINICAL_TRIALS trial_result · 2025-08-14

Clinical Trial Update: Ambroxol as a Disease-modifying Treatment in GBA-PD [Phase 2]

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Summary

Phase 2 trial evaluating ambroxol as a disease-modifying therapy for Parkinson disease with GBA mutation has completed.

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Diseases / indications

Drugs mentioned

  • Ambroxol (Ambroxol)

Snippet

Sponsor: Fondazione I.R.C.C.S. Istituto Neurologico Carlo Besta | Conditions: Parkinson Disease, GBA Gene Mutation | Phase 2 | Status: COMPLETED