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CLINICAL_TRIALS research · 2025-08-15

Clinical Trial Update: Decoding Central Defects in Dystrophinopathies From Diagnostic to Remediation

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Summary

Clinical trial update describing a study on central defects in dystrophinopathies, from diagnostic assessment to remediation strategies. The study is currently …

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Diseases / indications

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Sponsor: Assistance Publique - Hôpitaux de Paris | Conditions: Dystrophinopathies | Status: NOT_YET_RECRUITING