Clinical Trial Update: An Open Label Dose Escalation Study to Assess the Safety, Tolerability, and Pharmacologic Properties of High Dose Ambroxol Hydrochloride in Adult (≥ 18 Years of Age) Subjects With MPS III [Phase 2, Phase 3]

View source ↗

Summary

An open-label dose-escalation study (Phase 2/Phase 3) is evaluating the safety, tolerability, and pharmacologic properties of high-dose ambroxol hydrochloride i…

Upgrade for the full analysis, importance score, and drug timeline.

Diseases / indications

• Mucopolysaccharidosis Type Iii
• Sanfilippo Syndrome

Drugs mentioned

• Ambroxol hydrochloride (Ambroxol)

Snippet

Sponsor: Ozlem Goker-Alpan | Conditions: Sanfilippo Syndrome, MPS3 | Phase 2, Phase 3 | Status: RECRUITING