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CLINICAL_TRIALS research · 2025-08-22

Clinical Trial Update: Expanded Access/Compassionate Use of Rugonersen in Patients With Angelman Syndrome

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Summary

Expanded access/compassionate use program for Rugonersen in Angelman Syndrome is available.

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Diseases / indications

Drugs mentioned

  • Rugonersen (rugonersen)

Snippet

Sponsor: Oak Hill Bio Ltd | Conditions: Angelman Syndrome | Status: AVAILABLE