CLINICAL_TRIALS
trial_result
· 2025-08-24
Clinical Trial Update: A Study to Investigate the Safety, Tolerability, Pharmacokinetics (PK) and Pharmacodynamics (PD) of RO7248824 in Participants With Angelman Syndrome (AS) [Phase 1]
Summary
Phase 1 study evaluating safety, tolerability, pharmacokinetics and pharmacodynamics of RO7248824 in participants with Angelman Syndrome has completed.
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Diseases / indications
Drugs mentioned
Snippet
Sponsor: Hoffmann-La Roche | Conditions: Angelman Syndrome | Phase 1 | Status: COMPLETED