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CLINICAL_TRIALS trial_result · 2025-06-25

Clinical Trial Update: Pozelimab and Cemdisiran Combination Therapy in Adult Participants With Paroxysmal Nocturnal Hemoglobinuria Who Switch From Eculizumab Therapy [Phase 2]

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Summary

This Phase 2 trial assesses the combination of pozelimab and cemdisiran in adults with paroxysmal nocturnal hemoglobinuria who switched from eculizumab, with re…

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Diseases / indications

Drugs mentioned

  • Cemdisiran (cemdisiran)
  • Pozelimab

Snippet

Sponsor: Regeneron Pharmaceuticals | Conditions: Paroxysmal Nocturnal Hemoglobinuria | Phase 2 | Status: COMPLETED | Results posted: 2025-06-25