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CLINICAL_TRIALS ClinicalTrials.gov record update

A Two-Stage, Dose-Escalation and Safety & Efficacy Study of Bilateral Intraparenchymal Thalamic and Intracisternal/Intrathecal Administration of AXO-AAV-GM2 in Tay-Sachs or Sandhoff Disease

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Record identity and dates

Source
ClinicalTrials.gov
Source record ID
NCT04669535
Title field or adapter rule
protocolSection.identificationModule.officialTitle
Ingested At
2026-04-25T22:27:22.856872+00:00
Published At
2025-05-22T00:00:00+00:00
Record Updated At
2025-09-02
Results Posted At
2025-05-22
Timestamp Basis
source retrieval time was not retained by the feed adapter
Date limitation
source retrieval time was not retained by the feed adapter

Fields recorded by this source

protocolSection.conditionsModule.conditions
["Tay-Sachs Disease", "Sandhoff Disease"]
protocolSection.statusModule.lastUpdatePostDateStruct.date
"2025-09-02"
protocolSection.identificationModule.nctId
"NCT04669535"
protocolSection.identificationModule.officialTitle
"A Two-Stage, Dose-Escalation and Safety \u0026 Efficacy Study of Bilateral Intraparenchymal Thalamic and Intracisternal/Intrathecal Administration of AXO-AAV-GM2 in Tay-Sachs or Sandhoff Disease"
protocolSection.statusModule.overallStatus
"TERMINATED"
protocolSection.designModule.phases
["PHASE1"]
protocolSection.statusModule.resultsFirstPostDateStruct.date
"2025-05-22"

Study condition terms

  • Tay-Sachs Disease (protocolSection.conditionsModule.conditions)
  • Sandhoff Disease (protocolSection.conditionsModule.conditions)

Intervention details are not present in the imported fields for this record. No drug-condition relationship is inferred from co-listing.

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