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CLINICAL_TRIALS research · 2025-09-08

Clinical Trial Update: Study of BMN 349 Single Dose in PiZZ and PiMZ/MASH Adult Participants [Phase 1]

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Summary

A Phase 1 single-dose study of BMN 349 in adults with Alpha-1 antitrypsin deficiency is currently recruiting.

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Diseases / indications

Drugs mentioned

  • BMN 349

Snippet

Sponsor: BioMarin Pharmaceutical | Conditions: Alpha 1-Antitrypsin Deficiency | Phase 1 | Status: RECRUITING