CLINICAL_TRIALS
research
· 2025-09-08
Clinical Trial Update: Study of BMN 349 Single Dose in PiZZ and PiMZ/MASH Adult Participants [Phase 1]
Summary
A Phase 1 single-dose study of BMN 349 in adults with Alpha-1 antitrypsin deficiency is currently recruiting.
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Diseases / indications
Drugs mentioned
Snippet
Sponsor: BioMarin Pharmaceutical | Conditions: Alpha 1-Antitrypsin Deficiency | Phase 1 | Status: RECRUITING