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CLINICAL_TRIALS trial_result · 2025-09-09

Clinical Trial Update: SCID-X1 Gene Therapy Via Intravenous Lentiviral (Ivlv-X1) Injection [Phase 1, Phase 2]

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Summary

A Phase 1/2 clinical trial is evaluating an intravenous lentiviral gene therapy (Ivlv-X1) for X-linked severe combined immunodeficiency (SCID-X1); recruitment i…

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Diseases / indications

Drugs mentioned

  • Ivlv-X1 (lentiviral vector-based gene therapy for SCID-X1)

Snippet

Sponsor: Shenzhen Geno-Immune Medical Institute | Conditions: SCID, X-Linked | Phase 1, Phase 2 | Status: RECRUITING