CLINICAL_TRIALS
trial_result
· 2025-09-10
Clinical Trial Update: Expanded Access for ATB200/AT2221 for the Treatment of IOPD
Summary
Expanded Access for ATB200/AT2221 to treat infantile-onset Pompe disease is available, per the sponsor Amicus Therapeutics.
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Diseases / indications
Drugs mentioned
Snippet
Sponsor: Amicus Therapeutics | Conditions: Pompe Disease Infantile-Onset | Status: AVAILABLE