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CLINICAL_TRIALS trial_result · 2025-09-10

Clinical Trial Update: Expanded Access for ATB200/AT2221 for the Treatment of IOPD

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Summary

Expanded Access for ATB200/AT2221 to treat infantile-onset Pompe disease is available, per the sponsor Amicus Therapeutics.

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Diseases / indications

Drugs mentioned

  • ATB200/AT2221

Snippet

Sponsor: Amicus Therapeutics | Conditions: Pompe Disease Infantile-Onset | Status: AVAILABLE