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CLINICAL_TRIALS research · 2025-09-10

Clinical Trial Update: A Long-term Observational Study Evaluating Eteplirsen, Golodirsen, or Casimersen in Routine Clinical Practice

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Summary

This update describes a long-term observational study evaluating eteplirsen, golodirsen, and casimersen in routine clinical practice for Duchenne muscular dystr…

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Diseases / indications

Drugs mentioned

  • AMONDYS 45 (Casimersen)
  • EXONDYS 51 (eteplirsen)
  • VYONDYS 53 (golodirsen)

Snippet

Sponsor: Sarepta Therapeutics, Inc. | Conditions: Duchenne Muscular Dystrophy | Status: ENROLLING_BY_INVITATION