CLINICAL_TRIALS
research
· 2025-09-10
Clinical Trial Update: A Long-term Observational Study Evaluating Eteplirsen, Golodirsen, or Casimersen in Routine Clinical Practice
Summary
This update describes a long-term observational study evaluating eteplirsen, golodirsen, and casimersen in routine clinical practice for Duchenne muscular dystr…
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Diseases / indications
Drugs mentioned
Snippet
Sponsor: Sarepta Therapeutics, Inc. | Conditions: Duchenne Muscular Dystrophy | Status: ENROLLING_BY_INVITATION